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Spinal Muscular Atrophy Medical Research Study

If your child has been diagnosed with Spinal Muscular Atrophy (SMA), you face a number of tough decisions. And while you work to better understand the best medical options for your child, you are likely experiencing emotions like fear, confusion, anger, and sadness.

Because of the physical and emotional toll SMA can have on your life, it can seem like an endless battle, but you, and your child, are fighters.

Right now, treatments for SMA are limited, which leads many parents of SMA children to consider medical research studies. This research study is evaluating the safety and effectiveness of an investigational medication for children diagnosed with SMA.

If your child has been diagnosed with SMA and you are considering medical research as an option, click here to learn more about this study.

Is my child eligible?

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